Optimization of AAV Vector Genome Design for the Treatment of Motor Neuron Diseases

Time: 9:30 am
day: Conference Day Two

Details:

• Overview of the AAV gene therapy on SMA and ALS
• Optimized vector genome Improves the efficacy and safety of AAV9-mediated gene therapy for SMA
• Optimized artificial miRNAs by AAV9 vectors drastically improve survival and function in ALS mice

Speakers:

Jun Xie Jun is Associate Professor at the University of Massachusetts Medical School and Director, Vector Development of the Viral Vector Core. He has led the discovery Read more