De-Risking the Human Translatability Piece of Next-Generation Vectors
Time: 8:35 am
day: PRE-CONFERENCE WORKSHOP DAY
Details:
- Highlighting different approaches to produce robust, translatable data when transitioning through preclinical studies
- Better understanding disease mechanisms and anticipated clinical responses to guide vector selection and design
- Exploring more predictive preclinical models (e.g., human cells, organoids, assembloids) for both vector validation and development
- Outlining the role of vector bioengineering for fit-for-purpose human tissue types
- Reducing the number of animal model studies to lower costs, while maintaining good clinical translatability