Accelerating Clinical Impact with Novel AAV Vectors Designed for Enhanced Delivery to Eye, Muscle, & CNS
Time: 11:30 am
day: Conference Day One
Details:
- Applying AI to design AAV capsids with optimized transduction efficiency for eye, muscle, and CNS delivery to facilitate enhanced clinical outcomes
- Validating capsid performance in NHPs to ensure safety, efficacy, and effective translation of novel capsids
- Demonstrating delivery to specific cell populations to motivate accelerated development of more effective treatments for rare and common diseases