Accelerating Clinical Impact with Novel AAV Vectors Designed for Enhanced Delivery to Eye, Muscle, & CNS

Time: 11:30 am
day: Conference Day One

Details:

  • Applying AI to design AAV capsids with optimized transduction efficiency for eye, muscle, and CNS delivery to facilitate enhanced clinical outcomes
  • Validating capsid performance in NHPs to ensure safety, efficacy, and effective translation of novel capsids
  • Demonstrating delivery to specific cell populations to motivate accelerated development of more effective treatments for rare and common diseases

Speakers: